Article ID | Journal | Published Year | Pages | File Type |
---|---|---|---|---|
10145043 | Current Opinion in Biomedical Engineering | 2018 | 26 Pages |
Keywords
PEISFHRTFOPBAEZFNtransthyretindouble-stranded DNA breaksTTRSCFDMDNHEJRNPPNAHDRCRISPRDSBPACEPLGACRISPR/Cas9zinc finger nucleasesRNA interferencesingle guide RNARNAisgRNAPeptide nucleic acidHomology-directed repairTriplex-forming oligonucleotideclustered regularly interspaced short palindromic repeatNon-viral deliveryDuchenne muscular dystrophyribonucleoproteinTALENBBBblood brain barrierCMVnon-homologous end joiningStem Cell FactorNanoparticleWatson-Crickpoly(lactic-co-glycolic) acidpolyethyleneimine
Related Topics
Physical Sciences and Engineering
Engineering
Biomedical Engineering
Authors
Alexandra S. Piotrowski-Daspit, Peter M. Glazer, W. Mark Saltzman,