Article ID | Journal | Published Year | Pages | File Type |
---|---|---|---|---|
3813278 | New Horizons in Translational Medicine | 2015 | 8 Pages |
Keywords
CDESFNBBSAdeno-associated vectorAAVTUDCAIFTADPKDDDAVPRPE65Leber congenital amaurosisLCATauroursodeoxycholic acidRare diseaseautosomal dominant polycystic kidney diseaseintraflagellar transportDesmopressin acetateBardet–Biedl syndromeSulforaphaneCiliopathycommon data elementMIMMendelian Inheritance in ManGenetic disorderTranslational research
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Authors
Robert M. Haws, Anthony D. Krentz, Rachel V. Stankowski, Robert D. Steiner,