Article ID | Journal | Published Year | Pages | File Type |
---|---|---|---|---|
3840235 | Translational Research | 2013 | 6 Pages |
Abstract
Genetic correction of hemophilia A and B was long considered amenable to the available gene transfer technologies. This assumption has come to fruition with the recent results of a phase I/II trial for hemophilia B. Here we review the clinical application of gene therapy for the hemophilia's as a paradigm of the evolution of gene transfer science and technology. This review is not intended as comprehensive but rather to highlight current clinical developments of gene therapy for the hemophilias.
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Authors
Christopher E. Walsh, Katherine M. Batt,