Article ID | Journal | Published Year | Pages | File Type |
---|---|---|---|---|
6041464 | Neuromuscular Disorders | 2015 | 15 Pages |
Abstract
â¢An overview on the state-of-the-art of known and new biomarkers in DMD was presented.â¢The strategies to identify biomarkers using standard and novel technologies were compared.â¢The need to correlate outcome measures with biomarkers was established.â¢The relevance of dystrophin as biomarker in clinical trials was pointed out.â¢The importance of sharing data via registries and biorepositories was underlined.
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Authors
Alessandra Ferlini, Kevin M. Flanigan, Hanns Lochmuller, Francesco Muntoni, Peter A.C. 't Hoen, Elizabeth McNally,