Article ID | Journal | Published Year | Pages | File Type |
---|---|---|---|---|
8402087 | Advanced Drug Delivery Reviews | 2018 | 35 Pages |
Keywords
DEBLTRMLVRDEBinducible pluripotent stem cellsBMZX-SCIDEBsDDEBIPSCAAVPTCGMPADA-SCIDNHEJgRNAECMzinc-finger nucleasesDSBself-inactivatingSCCHDRZFNCRISPR/Cas9Small interfering RNArTMsiRNAdermal-epidermal junctionUltravioletHomology-directed repairWound HealingEpidermolysis bullosa simplexdystrophic epidermolysis bullosasinGood Manufacturing PracticeLong-terminal repeatJEBDEJguide RNATranscription activator-like effector nucleaseTALENStem cellsKindler syndromedouble strand breaksnon-homologous end-joiningExtracellular matrixBasement membrane zoneSMARTAdeno-associated virusMurine leukemia virusHIVgenodermatosesSquamous cell carcinomapremature termination codonX-linked severe combined immunodeficiencyjunctional epidermolysis bullosaepidermolysis bullosa
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Authors
Patricia Peking, Ulrich Koller, Eva M. Murauer,