Lysosomal enzyme replacement therapies: Historical development, clinical outcomes, and future perspectives

Article ID	Journal	Published Year	Pages	File Type
8402555	Advanced Drug Delivery Reviews	2017	63 Pages	PDF

Keywords

NPC M6PR FDA NPD M6P enzyme replacement therapy Side effects lysosomal storage disorders U.S. Food and Drug Administration Lysosomal disease Lysosomal diseases Neurodegeneration endoplasmic reticulum mannose-6-phosphate Mucopolysaccharidosis MPs wild-type ERT mannose-6-phosphate receptor

Related Topics

Life Sciences Biochemistry, Genetics and Molecular Biology Biotechnology

Lysosomal enzyme replacement therapies: Historical development, clinical outcomes, and future perspectives

Authors

Melani Solomon, Silvia Muro,