Article ID Journal Published Year Pages File Type
8952757 Paediatric Respiratory Reviews 2018 11 Pages PDF
Abstract
The number of published articles on Cystic Fibrosis (CF) continues to increase year on year. The evidence base for small molecule therapies in CF has continued to expand, with evidence for lumacaftor/ivacaftor in younger patients and longer-term evidence in adults, and pivotal studies on tezacaftor/ivacaftor. There were reports on emerging CFTR mutation agnostic therapies, and new evidence for long standing therapies.
Related Topics
Health Sciences Medicine and Dentistry Perinatology, Pediatrics and Child Health
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