Report on the workshop: Meaningful outcome measures for Duchenne muscular dystrophy, London, UK, 30-31 January 2017

- This report summarises discussion and data presented at a two day workshop on outcome measures for Duchenne muscular dystrophy.
- Participants included clinicians, industry, patient advocates and regulators.
- The focus is on the selection and use of clinical and imaging outcome measures.
- The inclusion of patient reported outcome measures is important.
- Data, information and best-practice sharing between stakeholders are necessary.