Article ID | Journal | Published Year | Pages | File Type |
---|---|---|---|---|
9232414 | Journal of Investigative Dermatology Symposium Proceedings | 2005 | 5 Pages |
Abstract
The ability to attract sufficient resources to effectively develop therapeutics for rare diseases is a daunting task. This review summarizes existing resources for rare diseases and discusses some of the challenges and strategies associated with developing therapies for small patient populations with an emphasis on pachyonychia congenita.
Related Topics
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Dermatology
Authors
Roger L. Kaspar,