Article ID | Journal | Published Year | Pages | File Type |
---|---|---|---|---|
10833113 | Molecular Genetics and Metabolism | 2013 | 7 Pages |
Abstract
In conclusion, ERT had an effect on several clinical parameters. This effect was established in an open cohort of young mucopolysaccharidosis type VI patients.
Keywords
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Biochemistry
Authors
Marion M.M.G. Brands, Esmee Oussoren, George J.G. Ruijter, Audrey A.M. Vollebregt, Hannerieke M.P. van den Hout, Koen F.M. Joosten, Wim C.J. Hop, Iris Plug, Ans T. van der Ploeg,