Article ID Journal Published Year Pages File Type
10833520 Molecular Genetics and Metabolism 2012 5 Pages PDF
Abstract
► ERT cessation results in a significant worsening of patients' clinical status. ► The negative effects of ERT cessation are more pronounced in MPS patients. ► Decisions about the introduction of ERT should be made carefully. ► Once started, it is essential to keep an adequate administration schedule of ERT.
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Related Topics
Life Sciences Biochemistry, Genetics and Molecular Biology Biochemistry
Preview
Effect of rapid cessation of enzyme replacement therapy: A report of 5 cases and a review of the literature
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