| Article ID | Journal | Published Year | Pages | File Type |
|---|---|---|---|---|
| 10833751 | Molecular Genetics and Metabolism | 2012 | 12 Pages |
Abstract
⺠We report the first experience with EPI-743, a novel redox drug, in treating mitochondrial disease. ⺠EPI-743 appears to be effective in altering the natural history of mitochondrial disease. ⺠Mitochondrial patients showed improvement in quality-of-life. ⺠Brain HMPAO SPECT scan results correlated with response to EPI-743 treatment ⺠Prospective controlled trials will be undertaken to substantiate these initial promising observations
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Authors
Gregory M. Enns, Stephen L. Kinsman, Susan L. Perlman, Kenneth M. Spicer, Jose E. Abdenur, Bruce H. Cohen, Akiko Amagata, Adam Barnes, Viktoria Kheifets, William D. Shrader, Martin Thoolen, Francis Blankenberg, Guy Miller,