Article ID | Journal | Published Year | Pages | File Type |
---|---|---|---|---|
5513895 | Molecular Genetics and Metabolism | 2017 | 20 Pages |
Abstract
Biomarker response after HCT is incomplete, which may reflect residual disease activity. Novel therapeutic strategies should aim for full metabolic correction to minimize clinical manifestations.
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Authors
Gé-Ann Kuiper, Peter M. van Hasselt, Jaap Jan Boelens, Frits A. Wijburg, Eveline J. Langereis,