Article ID Journal Published Year Pages File Type
8344030 Molecular Genetics and Metabolism 2012 5 Pages PDF
Abstract
► Bezafibrate decreased acylcarnitines in several FAO disorders in vitro. ► Bezafibrate improved abnormalities in a child with glutaric acidemia type 2. ► Bezafibrate is a promising treatment option for FAO disorders. ► In vitro probe assay can evaluate the effect of drugs to treat FAO disorders.
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Authors
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