Article ID | Journal | Published Year | Pages | File Type |
---|---|---|---|---|
8344030 | Molecular Genetics and Metabolism | 2012 | 5 Pages |
Abstract
⺠Bezafibrate decreased acylcarnitines in several FAO disorders in vitro. ⺠Bezafibrate improved abnormalities in a child with glutaric acidemia type 2. ⺠Bezafibrate is a promising treatment option for FAO disorders. ⺠In vitro probe assay can evaluate the effect of drugs to treat FAO disorders.
Keywords
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Authors
Seiji Yamaguchi, Hong Li, Jamiyan Purevsuren, Kenji Yamada, Midori Furui, Tomoo Takahashi, Yuichi Mushimoto, Hironori Kobayashi, Yuki Hasegawa, Takeshi Taketani, Toshiyuki Fukao, Seiji Fukuda,