Home treatment with intravenous enzyme replacement therapy with idursulfase for mucopolysaccharidosis type II

Article ID	Journal	Published Year	Pages	File Type
8344271	Molecular Genetics and Metabolism	2010	7 Pages	PDF

Abstract

Providing appropriate factors are considered, it should be feasible for patients with MPS II, including those who are severely affected, to receive infusions at home.

Keywords

IRR GAG CPAP I2S TIVAD BiPAP MPS II Mucopolysaccharidoses HOS Mucopolysaccharidosis type II enzyme replacement therapy Iduronate-2-sulfatase Infusion Home therapy Totally implantable venous access device Bi-level positive airway pressure Hunter syndrome Continuous positive airway pressure ERT Glycosaminoglycan

Related Topics

Life Sciences Biochemistry, Genetics and Molecular Biology Biochemistry

Preview

Home treatment with intravenous enzyme replacement therapy with idursulfase for mucopolysaccharidosis type II - data from the Hunter Outcome Survey

Authors

Barbara K. Burton, Nathalie Guffon, Jane Roberts, Ans T. van der Ploeg, Simon A. Jones, on behalf of the HOS investigators on behalf of the HOS investigators,