Preclinical and clinical development of siRNA-based therapeutics
Keywords: 2â²-OMe; 2â²-O-methyl; 2â²-F; 2â²-fluoro; CH/TA; chitosan/thioaptamer; DOPC; 1,2-dioleoyl-sn-glycero-3-phosphatidylcholine; DOTAP; 1,2-dioleoyl-3-trimethylammonium-propane; DOTMA; N-[1-(2,3-dioleoyloxy)propyl]-N,N,N-trimethylammonium methyl sulfate; E