Long-term regulation of gene expression in muscle cells by systemically delivered siRNA
Keywords: 2â²-F; 2â²-fluoro; 2â²OMe; 2â²-O-methyl; Ago; argonaute; AME; absorptive-mediated endocytosis; AMT; absorptive-mediated transcytosis; BBB; blood-brain barrier; BMB; blood-muscle barrier; BMD; Becker muscular dystrophy; CPP; cell penetrating peptid