
Gene therapy in cystic fibrosis
Keywords: AAV, adeno-associated viruses; AAV2, adeno-associated vector 2; CAR, coxsackie-adenovirus receptor; CF, cystic fibrosis; CFTR, cystic fibrosis transmembrane regulator; FEV1, forced expiratory volume in 1 s; NPD, nasal potential differences; PTC, premature