
Bone marrow transplantation improves outcome in a mouse model of congenital muscular dystrophy
Keywords: BMT, bone marrow transplantation; DMD, Duchenne muscular dystrophy; MDC1A, congenital muscular dystrophy type 1A; SpO2, arterial hemoglobin saturationBone marrow transplantation; Muscular dystrophy; mdx mouse; dy mouse; Laminin α2; Basal lamina