Long-term follow-up of IPEX syndrome patients after different therapeutic strategies: An international multicenter retrospective study
Keywords: IPEX; primary immune deficiency; FOXP3; Treg cells; hematopoietic stem cell transplantation; immunosuppression; rapamycin; enteropathy; neonatal diabetes; genetic autoimmunity; DFS; Disease-free survival; FKH; Forkhead domain; GvHD; Graft-versus-host dise