A new type of pharmacological chaperone for GM1-gangliosidosis related human lysosomal β-galactosidase: N-Substituted 5-amino-1-hydroxymethyl-cyclopentanetriols
Keywords: مهارکننده گالاکتوزیداز; Aminocyclopentane; Carbafuranose; Galactosidase inhibitor; Pharmacological chaperone; GM1-Gangliosidosis;