The effect of neonatal gene therapy on skeletal manifestations in mucopolysaccharidosis VII dogs after a decade
Keywords: (MPS); mucopolysaccharidosis; (GAGs); glycosaminoglycans; (DJD); degenerative joint disease; (TLR4); Toll-like receptor 4; (TNFα); tumor necrosis factor α; (MMP); matrix metalloproteinase; (HSCT); hematopoietic stem cell transplantation; (ERT); enzyme r