T-cell gene therapy for perforin deficiency corrects cytotoxicity defects and prevents hemophagocytic lymphohistiocytosis manifestations
Keywords: پنی سیلین و استرپتومایسین; Gene therapy; hemophagocytic lymphohistiocytosis; perforin deficiency; T cells; FHL; Familial hemophagocytic lymphohistiocytosis; GFP; Green fluorescent protein; HLH; Hemophagocytic lymphohistiocytosis; HSCT; Hematopoietic stem cell transplantation; IRES;