CRISPR Gene Editing in the Kidney
Keywords: بیماری کلیوی پلی کیستیک (PKD); CRISPR; gene editing; genome; organoids; polycystic kidney disease (PKD); nephrotic syndrome; human pluripotent stem cells (hPSC); chimeric antigen receptor T-cells (CAR-T); gene therapy; animal model; in vitro culture; gene knockout; review;