Use of polymer conjugates for the intraperoxisomal delivery of engineered human alanine:glyoxylate aminotransferase as a protein therapy for primary hyperoxaluria type I
Keywords: نوع اول هیپرکسالورژی اولیه; Protein therapeutics; Polymer conjugates; Primary hyperoxaluria; Rare disease; Peroxisomal targeting; Enzyme administration; PH1; primary hyperoxaluria type I; AGT; alanine:glyoxylate aminotransferase; PLP; pyridoxal 5â²-phosphate; PTS; peroxisomal targe