
A retrospective, multinational, multicenter study on the natural history of infantile-onset Pompe disease
Keywords: نسبت خطر; BiPAP; Bi-level positive airway pressure; CI; Confidence interval; CPAP; Continuous positive airway pressure; CRIM; Cross-reactive immunologic material; EKG; Electrocardiogram; GAA; α-Glucosidase; RR; Risk ratio; SD; Standard deviation;