Developing treatment for spinal and bulbar muscular atrophy
Keywords: AR, androgen receptor; HDAC, histone deacetylase; IGF-1, insulin-like growth factor 1; PI3K, phosphatidylinositol 3 kinase; SBMA, spinal and bulbar muscular atrophy; QMA, quantitative muscle assessmentSpinal and bulbar muscular atrophy; Kennedy's disease;