Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience

Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience

Database: Elsevier - ScienceDirect (ساینس دایرکت)
Journal: Neuromuscular Disorders - Volume 27, Issue 12, December 2017, Pages 1084-1086

Sonia Messina, Marika Pane, Valeria Sansone, Claudio Bruno, Michela Catteruccia, Giuseppe Vita, Concetta Palermo, Emilio Albamonte, Marina Pedemonte, Enrico Bertini, Luca Binetti, Eugenio Mercuri,