
Keywords: 3MSCT; 3-minute stair climb test; 6MWT; 6-minute walk test; AE; adverse event; ERT; enzyme replacement therapy; GALNS; enzyme N-acetylgalactosamine-6-sulfatase; IAR; infusion-associated reaction; IgE; immunoglobulin E; ITT; intent-to-treat; KS; keratan su