
Keywords: AAV; adeno-associated viruses; ADA; adenosine deaminase deficiency; APCs; antigen presenting cells; AuNC; gold nanoclusters; AuNPs; gold nanoparticles; AuNRs; gold nanorods; BBB; blood-brain barrier; Bcl-2; B-cell lymphoma 2; Cas; CRISPR-associated; ChNPs