Lentiviral Vectors That Express UGT1A1 in Liver and Contain miR-142 Target Sequences Normalize Hyperbilirubinemia in Gunn Rats
Keywords: فلورسانس فعال سلول مرتب ساز; Crigler-Najjar Syndrome; Gene Transfer; Lentivirus; MicroRNA; APC; antigen-presenting cells; CN-I; Crigler-Najjar type 1; FACS; fluorescence-activated cell sorter; GFP; green fluorescent protein; miRNA; microRNA; MOI; multiplicity of infection; PGK; p