The Morquio A Clinical Assessment Program: Baseline results illustrating progressive, multisystemic clinical impairments in Morquio A subjects

► MorCAP is the first natural history study with quantitative assessments of MPS IVA. ► Endurance, mobility, respiratory function, stature and quality of life are impacted. ► All affected individuals experience significant functional limitations. ► Increasing severity with age illustrates the progressive nature of Morquio A.