
Keywords: 1،2-dioleoyl-sn-glycero-3-phosphoethanolamine; AAV; adeno-associated viruses; ADA; adenosine deaminase deficiency; APCs; antigen presenting cells; AuNC; gold nanoclusters; AuNPs; gold nanoparticles; AuNRs; gold nanorods; BBB; blood-brain barrier; Bcl-2; B-cell lymphoma 2; Cas; CRISPR-associated; ChNPs