کد مقاله کد نشریه سال انتشار مقاله انگلیسی نسخه تمام متن
1999033 1065838 2007 4 صفحه PDF دانلود رایگان
عنوان انگلیسی مقاله ISI
Therapy for Gaucher disease: Don’t stop thinking about tomorrow
موضوعات مرتبط
علوم زیستی و بیوفناوری بیوشیمی، ژنتیک و زیست شناسی مولکولی زیست شیمی
پیش نمایش صفحه اول مقاله
Therapy for Gaucher disease: Don’t stop thinking about tomorrow
چکیده انگلیسی

While enzyme replacement therapy for Gaucher disease has been widely used and appears to be an efficacious and safe treatment, this success should not be a reason for complacency. Other treatment strategies currently under consideration for patients with Gaucher disease include gene therapy, substrate reduction therapy and chaperone therapy. Furthermore, improvements in enzyme therapy could also have a significant clinical impact. Individuals with Gaucher disease and other lysosomal disorders will greatly benefit from continual refinement and optimization of the current therapy, as well as from the development of new treatment modalities that offer improvements in efficacy, cost, safety and availability.

ناشر
Database: Elsevier - ScienceDirect (ساینس دایرکت)
Journal: Molecular Genetics and Metabolism - Volume 90, Issue 2, February 2007, Pages 122–125
نویسندگان
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