
Immune response after neonatal transfer of a human factor IX-expressing retroviral vector in dogs, cats, and mice
Keywords: داخل وریدی; FIX; Factor IX; IV; intravenous; hFIX; human FIX; RV; retroviral vector; MPS I; mucopolysaccharidosis I; CTL; cytotoxic T lymphocyte; cIDUA; canine α-l-iduronidase; WPRE; woodchuck hepatitis virus post-transcriptional regulatory element; IU; internationa